Chen (2022)

Colorectal Cancer

Oncology • Registry Data • US

Study Metrics
Covariates 4
PICO Comparisons 2
Quality Indicators
Transparency High
DAG Usage No
QBA Performed No

Study Information

First Author: Chen
Publication Year: 2022
DOI: https://doi.org/10.1200/cci.21.00195
Preprint: No preprint

Institution & Funding

Institution Type: Academic
Institutions: University of Florida, Cornell University, Duke University, Wake Forest School of Medicine
Funding: Declared: Public
Funding Institutions: Supported by National Cancer Institute R21CA253394; National Cancer Institute R01CA246418.

Study Context

Disease: Colorectal Cancer
Disease Category: Oncology
Data Type: Registry
Number of Data Sources: 1
Geography: US
Eligible Sample: 49948.0
Number of Emulations: 2
Number of Treatments: 2

Analytical Methods

Matching Method: PS matching
Analysis Method: Cox PH

Quality Methods

Directed Acyclic Graph (DAG) Not Used
Quantitative Bias Analysis (QBA) Not Performed

Target Trial Information

Target Trial Name: Cutsem et al.
Registration Number: NCT00154102
Target Trial DOI: https://doi.org/10.1200/jco.2010.33.5091

TTE vs RCT Comparisons

Detailed comparison between Target Trial Emulation results and corresponding Randomized Controlled Trial outcomes.

Death
Cutsem et al.
HR Efficacy
Population

Patients with metastatic colorectal cancer

Intervention

Cetuximab + FOLFIRI

Comparison

FOLFIRI alone

Outcome

Death

RCT Result

0.93

95% CI: [0.81, 1.07]


vs
TTE Result

0.86

95% CI: [0.68, 1.07]

Concordance Assessment
Confidence Interval Overlap: Yes
CIs overlap, suggesting concordance
Direction Agreement: Same Direction
Both point to similar conclusion
Death
Peeters et al.
HR Efficacy
Population

Patients with metastatic colorectal cancer

Intervention

Panitumumab + FOLFIRI

Comparison

FOLFIRI alone

Outcome

Death

RCT Result

0.96

95% CI: [0.75, 1.23]


vs
TTE Result

0.89

95% CI: [0.68, 1.38]

Concordance Assessment
Confidence Interval Overlap: Yes
CIs overlap, suggesting concordance
Direction Agreement: Same Direction
Both point to similar conclusion

Transparency Indicators

Protocol Registration Available
Data Sharing Not Available
Code Sharing Not Available
Overall Transparency Score:
High Transparency - This study meets good transparency standards.

Conflicts & Funding

Conflicts of Interest: Declared: Financial
COI Institutions: Tempus, Pfizer, Bristol Myers Squibb, Merck, AstraZeneca/MedImmune, Lilly, Bayer, Incyte, Ipsen, Seattle Genetics, Genentech, Astellas Pharma, BioMed Valley Discoveries, GlaxoSmithKline, Amgen, OncoC4, IBM, Boehringer Ingelheim, Synyi Tech, Air Liquide, Sanofi, Johnson & Johnson, Gilead Sciences, Celgene, Athenex
Funding Source: Declared: Public
Funding Institutions: Supported by National Cancer Institute R21CA253394; National Cancer Institute R01CA246418.