Robak (2024)

Chronic lymphocytic leukemia

Oncology • Other Data • Czech Republic, France

Study Metrics
Total Sample 811
Treatment Group 119
Control Group 692
Covariates 18
PICO Comparisons 1
Quality Indicators
Transparency High
DAG Usage No
QBA Performed No

Study Information

First Author: Robak
Publication Year: 2024
DOI: https://doi.org/10.1080/03007995.2024.2368175
Preprint: No preprint

Institution & Funding

Institutions: Medical University of Lodz, University Hospital Brno, Hôpital Lyon-Sud, Janssen Pharmaceutica NV, UAB "JOHNSON & JOHNSON", Janssen-Cilag GmbH, Janssen Sciences Ireland UC, Pharmacyclics
Funding: Declared: Private
Funding Institutions: The study was funded by Janssen Pharmaceutica NV and Pharmacyclics LLC, an AbbVie Company. The real-world databases in France and the Czech Republic (Lyon-Sud and CLLEAR) that were utilized are not owned by Janssen Pharmaceutica NV.

Study Context

Disease: Chronic lymphocytic leukemia
Disease Category: Oncology
Data Type: Other
Number of Data Sources: 2
Geography: Czech Republic, France
Eligible Sample: 1360.0
Number of Emulations: 3
Number of Treatments: 2

Analytical Methods

Matching Method: PS matching
Analysis Method: Cox PH

Quality Methods

Directed Acyclic Graph (DAG) Not Used
Quantitative Bias Analysis (QBA) Not Performed

Target Trial Information

Target Trial Name: RESONATE-2
Registration Number: NCT01722487
Target Trial DOI: https://doi.org/10.1056/nejmoa1509388, https://doi.org/10.3324/haematol.2018.192328

TTE vs RCT Comparisons

Detailed comparison between Target Trial Emulation results and corresponding Randomized Controlled Trial outcomes.

Overall survival
RESONATE-2
HR Efficacy
Population

Adult patients with chronic lymphocytic leukemia (CLL)

Intervention

First-line (1L) ibrutinib monotherapy

Comparison

First-line chemotherapy/chemoimmunotherapy (CT/CIT) followed by second-line (2L) ibrutinib after disease progression

Outcome

Overall survival

RCT Result

0.35

95% CI: [0.20, 0.62]


vs
TTE Result

0.64

95% CI: [0.39, 1.04]

Concordance Assessment
Confidence Interval Overlap: Yes
CIs overlap, suggesting concordance
Direction Agreement: Same Direction
Both point to similar conclusion

Transparency Indicators

Protocol Registration Available
Data Sharing Not Available
Code Sharing Not Available
Overall Transparency Score:
High Transparency - This study meets good transparency standards.

Conflicts & Funding

Conflicts of Interest: Declared: Financial
COI Institutions: Janssen, AbbVie, AstraZeneca, BeiGene, Lilly, AOP Orphan, Gilead
Funding Source: Declared: Private
Funding Institutions: The study was funded by Janssen Pharmaceutica NV and Pharmacyclics LLC, an AbbVie Company. The real-world databases in France and the Czech Republic (Lyon-Sud and CLLEAR) that were utilized are not owned by Janssen Pharmaceutica NV.