Merola (2023)

Breast cancer

Oncology • Ehr Data • US

Study Metrics
Total Sample 3836
Treatment Group 1299
Control Group 2537
Covariates 28
PICO Comparisons 1
Quality Indicators
Transparency High
DAG Usage No
QBA Performed No

Study Information

First Author: Merola
Publication Year: 2023
DOI: https://doi.org/10.1002/pds.5565
Preprint: No preprint

Institution & Funding

Institutions: Brigham and Women's Hospital, Harvard Medical School, Harvard TH Chan School of Public Health, Harvard Pilgrim Health Care Institute, Memorial Sloan Kettering Cancer Center, Weill Cornell Medical School, Massachusetts General Hospital, Avalere Health
Funding: Delcared: NGO
Funding Institutions: This project was funded by an Innovation in Regulatory Science Award from the Burroughs Wellcome Fund (#1020021).

Study Context

Disease: Breast cancer
Disease Category: Oncology
Data Type: Electronic Health Records
Number of Data Sources: 1
Geography: US
Eligible Sample: 3836.0

Analytical Methods

Missing Data Method: Multiple imputation
Matching Method: Stratification
Analysis Method: Cox PH

Quality Methods

Directed Acyclic Graph (DAG) Not Used
Quantitative Bias Analysis (QBA) Not Performed

Target Trial Information

Target Trial Name: PALOMA-2
Registration Number: NCT01740427
Target Trial DOI: https://doi.org/10.1007/s10549-018-05125-4

TTE vs RCT Comparisons

Detailed comparison between Target Trial Emulation results and corresponding Randomized Controlled Trial outcomes.

Time to next treatment (TTNT)
PALOMA-2
HR Efficacy
Population

Women aged ≥18 with hormone-positive, HER-2 negative metastatic breast cancer

Intervention

Palbociclib + letrozole

Comparison

Letrozole

Outcome

Time to next treatment (TTNT)

RCT Result

0.64

95% CI: [0.52, 0.78]


vs
TTE Result

0.62

95% CI: [0.56, 0.68]

Concordance Assessment
Confidence Interval Overlap: Yes
CIs overlap, suggesting concordance
Direction Agreement: Same Direction
Both point to similar conclusion

Transparency Indicators

Protocol Registration Available
Data Sharing Not Available
Code Sharing Not Available
Overall Transparency Score:
High Transparency - This study meets good transparency standards.

Conflicts & Funding

Conflicts of Interest: Declared: Financial
COI Institutions: Boehringer Ingelheim, Aetion Inc., McKesson Corporation
Funding Source: Delcared: NGO
Funding Institutions: This project was funded by an Innovation in Regulatory Science Award from the Burroughs Wellcome Fund (#1020021).