Merola (2022)

Breast cancer

Oncology • Ehr Data • US

Study Metrics
Total Sample 1886
Treatment Group 462
Control Group 1424
Covariates 18
PICO Comparisons 1
Quality Indicators
Transparency High
DAG Usage No
QBA Performed No

Study Information

First Author: Merola
Publication Year: 2022
DOI: https://doi.org/10.2147/CLEP.S373291
Preprint: No preprint

Institution & Funding

Institutions: Brigham and Women's Hospital, Harvard Medical School, Harvard TH Chan School of Public Health, Harvard Pilgrim Healthcare Institute, Memorial Sloan Kettering Cancer Center, Weill Cornell Medical School, Massachusetts General Hospital, Ontada
Funding: Declared: NGO
Funding Institutions: This project was funded by an Innovation in Regulatory Science Award from the Burroughs Wellcome Fund (#1020021).

Study Context

Disease: Breast cancer
Disease Category: Oncology
Data Type: Electronic Health Records
Number of Data Sources: 1
Geography: US
Eligible Sample: 1886.0

Analytical Methods

Missing Data Method: Multiple imputation
Matching Method: Stratification
Analysis Method: Cox PH

Quality Methods

Directed Acyclic Graph (DAG) Not Used
Quantitative Bias Analysis (QBA) Not Performed

Target Trial Information

Target Trial Name: PARSIFAL
Registration Number: NCT02491983
Target Trial DOI: https://doi.org/10.1001/jamaoncol.2021.4301

TTE vs RCT Comparisons

Detailed comparison between Target Trial Emulation results and corresponding Randomized Controlled Trial outcomes.

Overall survival
PARSIFAL
HR Efficacy
Population

Women ≥18 years old with metastatic breast cancer

Intervention

Fulvestrant + Palbociclib

Comparison

Letrozole + Palbociclib

Outcome

Overall survival

RCT Result

1.00

95% CI: [0.68, 1.48]


vs
TTE Result

1.07

95% CI: [0.86, 1.35]

Concordance Assessment
Confidence Interval Overlap: Yes
CIs overlap, suggesting concordance
Direction Agreement: Different Direction
Different conclusions

Transparency Indicators

Protocol Registration Available
Data Sharing Not Available
Code Sharing Not Available
Overall Transparency Score:
High Transparency - This study meets good transparency standards.

Conflicts & Funding

Conflicts of Interest: Declared: Financial
COI Institutions: Aetion Inc, McKesson Corporation, Boehringer Ingelheim, JAMA, GRAIL, Dana-Farber Cancer Institute
Funding Source: Declared: NGO
Funding Institutions: This project was funded by an Innovation in Regulatory Science Award from the Burroughs Wellcome Fund (#1020021).