TTE vs RCT Comparisons

Studies that directly compared Target Trial Emulation results with their corresponding Randomized Controlled Trials. Explore 28 comparative studies examining concordance patterns.

28
Comparative Studies

Baptiste (2024)

Disease: Cardiovascular disease (Cardiology)
Data: Ehr from UK
Sample Size: 137155 (Treatment: 40553, Control: 96602)

PS matching Cox PH
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Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
ONTARGET ≥30% increase in serum creatinine Efficacy RR 1.14
[0.80, 1.62]
1.38
[1.34, 1.43]
CI Overlap
Same Direction
ONTARGET Angioedema Efficacy RR 0.40
[0.19, 0.86]
1.14
[0.72, 1.80]
CI Overlap
Different Direction
ONTARGET Cough Efficacy RR 0.26
[0.21, 0.33]
1.29
[1.16, 1.43]
No Overlap
Different Direction
ONTARGET Death from any cause Efficacy HR 0.98
[0.90, 1.07]
0.97
[0.93, 1.01]
CI Overlap
Same Direction
ONTARGET Death from cardiovascular causes Efficacy HR 1.00
[0.89, 1.12]
0.96
[0.90, 1.03]
CI Overlap
Different Direction
ONTARGET Death from non-cardiovascular causes Efficacy HR 0.96
[0.83, 1.10]
0.97
[0.92, 1.02]
CI Overlap
Same Direction
ONTARGET Hospitalisation for heart failure Efficacy HR 1.12
[0.97, 1.29]
0.97
[0.90, 1.05]
CI Overlap
Different Direction
ONTARGET Main secondary outcome: Death from card… Efficacy HR 0.99
[0.91, 1.07]
0.98
[0.94, 1.02]
CI Overlap
Same Direction
ONTARGET Myocardial infarction Efficacy HR 1.07
[0.94, 1.22]
0.97
[0.92, 1.01]
CI Overlap
Different Direction
ONTARGET Primary composite: Death from cardiovas… Efficacy HR 1.01
[0.94, 1.09]
0.98
[0.94, 1.02]
CI Overlap
Different Direction
ONTARGET Stroke Efficacy HR 0.91
[0.79, 1.05]
1.04
[0.97, 1.12]
CI Overlap
Different Direction

Goriacko (2024)

Disease: COVID-19 (Infectious diseases)
Data: Ehr from US
Sample Size: 716 (Treatment: 244, Control: 472)

DAG Coarsened exact matching Logistic regre…
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TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
REMAP-CAP 28-day all-cause mortality Efficacy OR 0.76
[0.66, 0.88]
0.86
[0.52, 1.44]
CI Overlap
Same Direction

Matthews (2024)

Disease: Myocardial infarction (Cardiology)
Data: Registry from Sweden
Sample Size: 10926 (Treatment: 9728, Control: 1198)

IPTW Logistic regre…
High Transparency
Protocol Available Code Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
REDUCE-AMI death or recurrent myocardial infarction Efficacy HR 0.96
[0.79, 1.16]
0.78
[0.59, 1.12]
CI Overlap
Same Direction

Robak (2024)

Disease: Chronic lymphocytic leukemia (Oncology)
Data: Other from Czech Republic, France
Sample Size: 811 (Treatment: 119, Control: 692)

PS matching Cox PH
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TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
RESONATE-2 Overall survival Efficacy HR 0.35
[0.20, 0.62]
0.64
[0.39, 1.04]
CI Overlap
Same Direction

Signori (2024)

Disease: Multiple sclerosis (Neurology)
Data: Registry from Italy, Australia, Turkey, Czech Republic, Kuwait, Switzerland, Spain, Lebanon, Canada
Sample Size: 4376 (Treatment: 3236, Control: 1140)

1:1 PS matching Negative binom…
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TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
TRANSFORMS Annual relapse rate Efficacy RR 0.49
[0.37, 0.64]
0.55
[0.45, 0.68]
CI Overlap
Same Direction

Szmulewicz (2024)

Disease: Psychosis (Psychology)
Data: Other from US, Canada, Spain
Sample Size: 1236 (Treatment: 853, Control: 383)

IPTW Cox PH, Logist…
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TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
EUFEST 12-month risks of discontinuation Efficacy HR 0.52
[0.36, 0.76]
0.41
[0.28, 0.59]
CI Overlap
Same Direction
EUFEST Admission to hospital after intake Efficacy RR 1.05
[0.80, 1.36]
1.11
[0.78, 1.59]
CI Overlap
Same Direction
EUFEST Co-prescription of antidepressants Efficacy RR 0.33
[0.21, 0.54]
0.81
[0.54, 1.21]
No Overlap
Same Direction
EUFEST Co-prescription of mood stabilizers Efficacy RR 1.00
[0.77, 1.30]
1.74
[1.03, 2.92]
CI Overlap
Different Direction
EUFEST Overall functioning score (GAF) Efficacy MD -0.10
[-9.80, 9.70]
2.70
[-3.84, 9.24]
CI Overlap
Different Direction
EUFEST Severity of illness score (CGI-S) Efficacy MD -0.10
[-0.93, 0.73]
-0.50
[-0.92, -0.08]
CI Overlap
Same Direction

Evans (2023)

Disease: Blood infection (Hematology)
Data: Other from UK
Sample Size: 121 (Treatment: 82, Control: 39)

PS matching Logistic regre…
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Protocol Available Data Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
MERINO all-cause mortality at 25 days Efficacy OR 3.69
[1.48, 10.40]
1.31
[0.40, 4.26]
CI Overlap
Same Direction

Gallivan (2023)

Disease: Neovascular age-related macular degeneration (Opthalmology)
Data: Ehr from Ireland
Sample Size: 4303 (Treatment: 1783, Control: 2520)

inverse-odds-of-sampling ANOVA
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Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
VIEW 1 Mean change in ETDRS BCVA letters Efficacy MD 0.50
[-1.69, 2.69]
-1.30
[-4.91, 2.31]
CI Overlap
Different Direction

Merola (2023)

Disease: Breast cancer (Oncology)
Data: Ehr from US
Sample Size: 3836 (Treatment: 1299, Control: 2537)

Stratification Cox PH
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TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
PALOMA-2 Time to next treatment (TTNT) Efficacy HR 0.64
[0.52, 0.78]
0.62
[0.56, 0.68]
CI Overlap
Same Direction

Wakabayashi (2023)

Disease: Diabetes (Endocrinology)
Data: Other from Japan
Sample Size: 96 (Treatment: 48, Control: 48)

1:1 PS nearest-neighbor matching t-distribution
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Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
COMPASS Change in HbA1c, % Efficacy MD -0.28
[-0.14, -0.16]
-0.01
[-0.25, 0.23]
CI Overlap
Same Direction
Onishi 2013 et al. Change in HbA1c, % Efficacy MD -0.28
[-0.46, -0.10]
0.46
[-0.01, 0.94]
No Overlap
Different Direction
PRIME-V Percentage changes in HbA1c levels (%) Efficacy MD 4.03
[0.79, 7.27]
-6.21
[-11.01, -1.40]
No Overlap
Different Direction

Wang (2023)

Disease: Multiple conditions including cardiovascular outcomes, diabetes, antiplatelet agents, anticoagulants, hypertension, osteoporosis, kidney disease, heart failure, asthma, COPD, and prostate cancer (All areas)
Data: Claims from US

PS matching Cox PH
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TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
ISAR-REACT 5 All cause death, non-fatal myocardial i… Efficacy HR 1.36
[1.09, 1.70]
Not available Cannot assess
P04334 Asthma exacerbation Efficacy HR 0.54
[0.44, 0.72]
0.78
[0.62, 0.97]
CI Overlap
Same Direction
D5896 Asthma related death, intubation, hospi… Efficacy HR 1.07
[0.70, 1.65]
1.38
[0.90, 2.13]
CI Overlap
Same Direction
CARMELINA Composite of nonfatal stroke, nonfatal … Efficacy HR 1.02
[0.89, 1.17]
0.90
[0.84, 0.96]
CI Overlap
Different Direction
SAVOR-TIMI Composite of nonfatal stroke, nonfatal … Efficacy HR 1.00
[0.89, 1.12]
0.81
[0.76, 0.86]
No Overlap
Different Direction
TRITON-TIMI Composite of nonfatal stroke, nonfatal … Efficacy HR 0.81
[0.73, 0.90]
0.88
[0.79, 0.97]
CI Overlap
Same Direction
PLATO Composite of nonfatal stroke, nonfatal … Efficacy HR 0.84
[0.77, 0.92]
0.92
[0.83, 1.02]
CI Overlap
Same Direction
LEADER Composite of nonfatal stroke, nonfatal … Efficacy HR 0.87
[0.78, 0.97]
0.82
[0.76, 0.87]
CI Overlap
Same Direction
EMPA-REG Composite of nonfatal stroke, nonfatal … Efficacy HR 0.86
[0.74, 0.99]
0.83
[0.73, 0.95]
CI Overlap
Same Direction
CANVAS Composite of nonfatal stroke, nonfatal … Efficacy HR 0.86
[0.75, 0.97]
0.77
[0.70, 0.85]
CI Overlap
Same Direction
CAROLINA Composite of nonfatal stroke, nonfatal … Efficacy HR 0.95
[0.84, 1.14]
0.91
[0.79, 1.05]
CI Overlap
Same Direction
PRONOUNCE Composite of nonfatal stroke, nonfatal … Efficacy HR 1.28
[0.59, 2.79]
1.35
[0.94, 1.93]
CI Overlap
Same Direction
TECOS Composite of nonfatal stroke, nonfatal … Efficacy HR 0.98
[0.88, 1.09]
0.89
[0.86, 0.91]
CI Overlap
Same Direction
ONTARGET Composite of nonfatal stroke, nonfatal … Efficacy HR 1.01
[0.94, 1.09]
0.83
[0.77, 0.90]
No Overlap
Different Direction
TRANSCEND Composite of nonfatal stroke, nonfatal … Efficacy HR 0.92
[0.81, 1.05]
0.88
[0.83, 0.96]
CI Overlap
Same Direction
INSPIRE COPD exacerbation Efficacy HR 0.97
[0.84, 1.12]
0.93
[0.90, 0.96]
CI Overlap
Same Direction
RECORD1 Deep vein thrombosis, pulmonary embolis… Efficacy HR 0.25
[0.14, 0.47]
0.17
[0.10, 0.29]
CI Overlap
Same Direction
DAPA-CKD End stage renal disease / death Efficacy HR 0.61
[0.51, 0.72]
0.80
[0.52, 1.26]
CI Overlap
Same Direction
LEAD-2 Hemoglobin A1c Efficacy MD Not available 0.05
[-0.11, 0.22]
Cannot assess
HORIZON-PFT Hip Fracture Efficacy HR 0.59
[0.42, 0.83]
0.72
[0.55, 0.94]
CI Overlap
Same Direction
DECLARE-TIMI58 Hospitalization for heart failure + car… Efficacy HR 0.83
[0.73, 0.95]
0.69
[0.59, 0.81]
CI Overlap
Same Direction
PARADIGM-HF Hospitalization for heart failure / mor… Efficacy HR 0.80
[0.73, 0.87]
1.02
[0.91, 1.14]
No Overlap
Different Direction
IMPACT Moderate or severe COPD exacerbation Efficacy HR 0.85
[0.80, 0.90]
1.13
[1.04, 1.23]
No Overlap
Different Direction
POET-COPD Moderate or severe COPD exacerbation Efficacy HR 0.83
[0.77, 0.90]
1.02
[0.93, 1.12]
No Overlap
Different Direction
RE-LY Stroke/Systemic Embolism Efficacy HR 0.66
[0.53, 0.82]
0.73
[0.60, 0.90]
CI Overlap
Same Direction
ROCKET AF Stroke/Systemic Embolism Efficacy HR 0.79
[0.66, 0.96]
0.70
[0.62, 0.80]
CI Overlap
Same Direction
ARISTOTLE Stroke/Systemic Embolism Efficacy HR 0.79
[0.66, 0.95]
0.68
[0.61, 0.76]
CI Overlap
Same Direction
EINSTEIN PE Venous thromboembolism Efficacy HR 1.12
[0.75, 1.68]
0.67
[0.55, 0.80]
CI Overlap
Different Direction
EINSTEIN DVT Venous thromboembolism Efficacy HR 0.68
[0.44, 1.04]
0.75
[0.62, 0.90]
CI Overlap
Same Direction
AMPLIFY Venous thromboembolism / Venous thrombo… Efficacy HR 0.84
[0.60, 1.18]
0.81
[0.54, 1.23]
CI Overlap
Same Direction
RE-COVER II Venous thromboembolism / Venous thrombo… Efficacy HR 1.08
[0.64, 1.80]
1.15
[0.74, 1.78]
CI Overlap
Same Direction
VERO Vertebral fracture Efficacy HR 0.44
[0.29, 0.68]
Not available Cannot assess

Barbulescu (2022)

Disease: Rheumatoid Arthritis (Rheumatology)
Data: National_Database from Sweden
Sample Size: 509 (Treatment: 313, Control: 196)

IPTW logistic regre…
High Transparency
Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
SWEFOT European Alliance of Associations for R… Efficacy RR 1.22
[0.98, 1.53]
1.27
[0.99, 1.63]
CI Overlap
Same Direction
SWEFOT European Alliance of Associations for R… Efficacy RR 1.59
[1.10, 2.30]
1.48
[0.98, 2.24]
CI Overlap
Same Direction

Chen (2022)

Disease: Colorectal Cancer (Oncology)
Data: Registry from US

PS matching Cox PH
High Transparency
Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
Cutsem et al. Death Efficacy HR 0.93
[0.81, 1.07]
0.86
[0.68, 1.07]
CI Overlap
Same Direction
Peeters et al. Death Efficacy HR 0.96
[0.75, 1.23]
0.89
[0.68, 1.38]
CI Overlap
Same Direction

Hou (2022)

Disease: Colorectal Cancer (Oncology)
Data: Ehr from US
Sample Size: 943 (Treatment: 518, Control: 425)

PS matching Cox PH
High Transparency
Protocol Available Code Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
COST 5-year overall survival Efficacy RD 0.01
[-0.17, 0.18]
-0.01
[-0.07, 0.06]
CI Overlap
Different Direction

Jang (2022)

Disease: Relapsed/refractory multiple myeloma (Oncology)
Data: Other from South Korea
Sample Size: 138 (Treatment: 69, Control: 69)

PS Matching, 1:1 matching Cox PH
High Transparency
Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
EMPA-REG OUTCOME Acute kidney injury Efficacy OR 0.78
[0.63, 0.96]
0.70
[0.59, 0.82]
CI Overlap
Same Direction
ASPIRE Acute renal failure Efficacy RR 1.19
[0.70, 2.00]
1.30
[0.53, 3.16]
CI Overlap
Same Direction
EMPA-REG OUTCOME All cause death Efficacy HR 0.68
[0.57, 0.82]
0.78
[0.67, 0.91]
CI Overlap
Same Direction
EMPA-REG OUTCOME Coronary revascularization Efficacy HR 0.86
[0.72, 1.04]
0.94
[0.87, 1.02]
CI Overlap
Same Direction
ASPIRE Cough Efficacy RR 1.94
[1.37, 2.72]
1.04
[0.45, 2.45]
CI Overlap
Same Direction
EMPA-REG OUTCOME Diabetic ketoacidosis Efficacy OR 1.99
[0.20, 17.80]
1.09
[0.72, 1.64]
CI Overlap
Same Direction
ASPIRE Diarrhea Efficacy RR 1.44
[1.08, 1.92]
1.03
[0.52, 1.99]
CI Overlap
Same Direction
ASPIRE Dyspenia Efficacy RR 1.38
[0.94, 2.00]
2.27
[1.24, 4.16]
CI Overlap
Same Direction
EMPA-REG OUTCOME Fracture Efficacy OR 0.98
[0.76, 1.27]
0.94
[0.87, 1.03]
CI Overlap
Same Direction
EMPA-REG OUTCOME Genital infection Efficacy OR 3.74
[2.70, 5.19]
1.49
[1.35, 1.65]
No Overlap
Same Direction
ASPIRE Heart failure Efficacy RR 1.59
[0.83, 3.02]
1.45
[0.61, 3.48]
CI Overlap
Same Direction
EMPA-REG OUTCOME hospitalization for heart failure Efficacy HR 0.65
[0.50, 0.85]
0.85
[0.75, 0.95]
CI Overlap
Same Direction
EMPA-REG OUTCOME Hospitalization for unstable angine Efficacy HR 0.99
[0.74, 1.34]
0.94
[0.88, 1.01]
CI Overlap
Same Direction
ASPIRE Hypertension Efficacy RR 2.23
[1.38, 3.62]
1.32
[0.73, 2.40]
CI Overlap
Same Direction
EMPA-REG OUTCOME Hypoglycemic adverse event Safety OR 1.00
[0.89, 1.11]
0.70
[0.59, 0.84]
No Overlap
Different Direction
ASPIRE Hypokalemia Efficacy RR 2.46
[1.69, 3.57]
1.91
[0.62, 5.87]
CI Overlap
Same Direction
ASPIRE Ischemic heart disease Efficacy RR 1.28
[0.68, 2.42]
1.00
[0.34, 2.92]
CI Overlap
Different Direction
EMPA-REG OUTCOME MACE (major adverse cardiovascular even… Safety HR 0.86
[0.74, 0.99]
0.87
[0.79, 0.96]
CI Overlap
Same Direction
ASPIRE Muscle spasm Efficacy RR 1.36
[0.97, 1.89]
5.12
[1.05, 15.00]
CI Overlap
Same Direction
EMPA-REG OUTCOME Myocardial infarction Efficacy HR 0.87
[0.70, 1.09]
0.91
[0.76, 1.08]
CI Overlap
Same Direction
ASPIRE Pyrexia Efficacy RR 1.52
[1.08, 2.11]
1.79
[0.97, 3.24]
CI Overlap
Same Direction
EMPA-REG OUTCOME Stroke Efficacy HR 1.18
[0.89, 1.56]
0.89
[0.75, 1.05]
CI Overlap
Different Direction
ASPIRE Thrombocytopenia Efficacy RR 1.40
[1.02, 1.94]
1.84
[1.10, 3.06]
CI Overlap
Same Direction
EMPA-REG OUTCOME Thromboembolic event Efficacy OR 0.75
[0.42, 1.31]
0.92
[0.80, 1.05]
CI Overlap
Same Direction
EMPA-REG OUTCOME Transient ischemic attack Efficacy HR 0.85
[0.51, 1.42]
0.88
[0.74, 1.04]
CI Overlap
Same Direction
ASPIRE Upper respiratory tract infection Efficacy RR 1.68
[1.19, 2.33]
1.43
[0.59, 3.56]
CI Overlap
Same Direction
EMPA-REG OUTCOME Urinary tract infection Efficacy OR 0.99
[0.87, 1.13]
0.87
[0.81, 0.94]
CI Overlap
Same Direction
EMPA-REG OUTCOME Volume depletion Efficacy OR 1.04
[0.82, 1.30]
0.84
[0.76, 0.94]
CI Overlap
Different Direction

Jin (2022)

Disease: Osteoarthritis (Rheumatology)
Data: Registry from US
Sample Size: 1566 (Treatment: 237, Control: 1329)

IPTW Hierarchical l…
High Transparency
Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
Sanghi et al., McAlindon et a… Change in WOMAC function score at 24 mo… Efficacy SMD -0.92
[-1.32, -0.51]
0.02
[-0.11, 0.15]
No Overlap
Different Direction
Sanghi et al., McAlindon et a… Change in WOMAC pain score at 24 months Efficacy SMD -0.39
[-0.78, 0.00]
0.08
[-0.07, 0.23]
CI Overlap
Different Direction

Kuehne (2022)

Disease: Ovarian cancer (Oncology)
Data: Other from US
Sample Size: 3164 (Treatment: 1582, Control: 1582)

DAG Cox PH
High Transparency
Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
MRC OV05/EORTC 55955 Overall survival Efficacy HR 1.01
[0.82, 1.25]
1.12
[0.96, 1.28]
CI Overlap
Same Direction

Matthews (2022)

Disease: Myocardial infarction (Cardiology)
Data: Registry from Sweden
Sample Size: 18222 (Treatment: 3462, Control: 14760)

Not defined Cox PH
High Transparency
Protocol Available Code Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
TASTE Death Efficacy RR 0.94
[0.78, 1.15]
1.09
[0.96, 1.24]
CI Overlap
Different Direction
TASTE Myocardial infarction Efficacy RR 0.97
[0.73, 1.28]
0.96
[0.79, 1.17]
CI Overlap
Same Direction

Merola (2022)

Disease: Breast cancer (Oncology)
Data: Ehr from US
Sample Size: 1886 (Treatment: 462, Control: 1424)

Stratification Cox PH
High Transparency
Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
PARSIFAL Overall survival Efficacy HR 1.00
[0.68, 1.48]
1.07
[0.86, 1.35]
CI Overlap
Different Direction

Softness (2022)

Disease: Bladder cancer (Oncology)
Data: National_Database from US
Sample Size: 2048 (Treatment: 1812, Control: 236)

IPTW Cox PH
High Transparency
Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
SPARE Overall survival Efficacy HR 3.05
[0.92, 10.15]
0.87
[0.64, 1.19]
CI Overlap
Different Direction

Matthews (2021)

Disease: Myocardial infarction (Cardiology)
Data: Registry from Sweden
Sample Size: 4940 (Treatment: 2634, Control: 2306)

IPTW logistic regre…
High Transparency
Protocol Available Code Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
VALIDATE Composite of death from any cause, MI, … Efficacy RR 0.96
[0.83, 1.10]
0.93
[0.77, 1.12]
CI Overlap
Same Direction
VALIDATE Death by 180 days Efficacy RR 1.05
[0.78, 1.41]
1.21
[0.88, 1.68]
CI Overlap
Same Direction
VALIDATE Major bleeding by 180 days Efficacy RR 1.00
[0.84, 1.19]
0.69
[0.50, 0.95]
CI Overlap
Different Direction
VALIDATE MI by 180 days Efficacy RR 0.84
[0.60, 1.19]
1.08
[0.76, 1.54]
CI Overlap
Different Direction

Weberpals (2021)

Disease: Advanced non-small cell lung cancer (Oncology)
Data: Ehr from US

1:1 PS matching Cox PH
High Transparency
Protocol Available Code Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
PRONOUNCE Overall survival Efficacy HR 1.07
[0.83, 1.36]
1.09
[0.87, 1.37]
CI Overlap
Same Direction

Yiu (2021)

Disease: Psoriasis (Immunology)
Data: Registry from UK and Ireland
Sample Size: 1231 (Treatment: 314, Control: 917)

PS weighted Generalized li…
High Transparency
Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
CLEAR PASI<=2 after 12 months Efficacy RR 1.24
[1.11, 1.37]
1.28
[1.06, 1.55]
CI Overlap
Same Direction

Althunian (2020)

Disease: Atrial fibrilation (Cardiology)
Data: National_Database from UK
Sample Size: 25473 (Treatment: 4008, Control: 21465)

Cox PH
High Transparency
Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
Rocket AF major bleeding Efficacy HR 1.04
[0.90, 1.20]
1.07
[0.95, 1.21]
CI Overlap
Same Direction
Rocket AF stroke, systemic emoblism, death Efficacy HR 0.86
[0.74, 0.99]
1.18
[1.03, 1.34]
No Overlap
Different Direction
Rocket AF stroke, systemic emoblism prevention Efficacy HR 0.88
[0.75, 1.03]
1.04
[0.84, 1.30]
CI Overlap
Different Direction

Bacic (2020)

Disease: Renal cell carcinoma (Oncology)
Data: Other from US
Sample Size: 67388 (Treatment: 58815, Control: 8573)

PS matching Cox PH
High Transparency
Protocol Available

TTE vs RCT Comparisons
Target Trial Outcome Effect Measure RCT Result TTE Result Concordance
EORTC 30881 Overall survival Efficacy HR 1.02
[0.80, 1.29]
1.13
[1.07, 1.20]
CI Overlap
Same Direction

About TTE vs RCT Comparisons

This page showcases studies that directly compared Target Trial Emulation (TTE) results with their corresponding Randomized Controlled Trials (RCTs). These comparisons are crucial for understanding the validity and reliability of the TTE methodology.

Key Metrics:
  • CI Overlap: Whether confidence intervals of TTE and RCT estimates overlap
  • Direction Agreement: Whether TTE and RCT point to the same conclusion (benefit/harm)
  • Effect Measure: The statistical measure used (HR, OR, RR, etc.)
  • Transparency: Availability of protocol, data, and analysis code
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Studies with RCT Comparisons